Gene Therapy Shows Promise for Rare Immune Disorder

April 22, 2015 4:00 PM

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WEDNESDAY, April 22, 2015 (HealthDay News) -- Gene therapy may benefit children and teens with a rare immune disorder called Wiskott-Aldrich syndrome, a small study finds.

The disorder -- characterized by low blood platelet count, eczema and recurring infections -- is caused by mutations in what's known as the WAS gene. People with the disorder generally die by their 20s or 30s. Blood stem cell transplants from other people can help these patients, but they have a hig...

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