Gene therapy effective to treat 'bubble boy' syndrome

October 9, 2014 1:27 AM

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Gene therapy effective to treat 'bubble boy' syndrome

An advance in gene therapy may provide safe treatment to children with a fatal genetic disorder that leads to no functioning immune system.

The majority of children with X-linked severe combined immunodeficiency, or X-SCID, die before the age of one and must live in a "bubble" for protection.

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