FDA Approves New Drug for Rare Genetic Disease

August 20, 2014 12:08 AM

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WASHINGTON (AP) — The Food and Drug Administration on Tuesday approved a new capsule-based drug to treat Gaucher’s disease.

Regulators approved the new drug, Cerdelga, for patients with the Type 1 form of the rare genetic disorder, which causes excess fat to build up in the spleen, liver and bone marrow.

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